Comment by JohnMakin

I have an extremely rare autosomal dominant subtype of a certain genetic disorder that affects maybe less than a few thousand individuals at any one time in the USA. Much common versions of the disorder that affect children have been successfully treated/cured with gene therapy. However gene treatment unlikely to ever reach people like me because so few are affected by it, it's not viable commercially. It's extremely frustrating and I struggle with tremendous feelings of anger about it, but I can't really do anything short of become a billionaire and fund my own treatment. Such is the state of medicine for profit, I guess.